2018 preview: Gene therapy treats disease while in the womb

时间:2019-03-07 02:11:01166网络整理admin

Dr G. Moscoso/Science Photo Library By Andy Coghlan “You can see during pregnancy that they already have bone fractures in the womb,” says Cecilia Götherström of the Karolinska Institute in Stockholm, Sweden. She is head of what will be the world’s first ever trial of giving fetuses stem cell therapy in the womb. The aim is to relieve symptoms of, or even cure, osteogenesis imperfecta, known as brittle bone disease. Babies born with this rare condition have bones that fracture easily, caused by having faulty genes for collagen,